BBM-H901 was shown to significantly reduce bleeding rates among hemophilia B patients in clinical trials, a new study in ...
The US FDA has approved the first ever cell-based gene therapy to treat Wiskott-Aldrich syndrome (WAS).
The first infant to undergo gene-editing therapy has accomplished another first — his first steps. KJ Muldoon is walking and ...
Bayer AG ($BAYRY) announced an update on their ongoing clinical study. Study Overview The PROGRESS-GT LOPD trial is an early-stage clinical study ...
The U.S. Food and Drug Administration said on Tuesday it had approved the first gene therapy for a rare and life-threatening ...
An activity pattern in certain genes responsible for building proteins known as spleen tyrosine kinases can predict which melanoma patients are likely to have severe side effects from immunotherapy ...
The effects allowed these minors who could sit but not stand to move like they've never done before, including walking and ...
Fondazione Telethon announced today that the U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) ...
Fondazione Telethon ETS' Waskyra has become the first gene therapy in the US for patients with Wiskott-Aldrich syndrome (WAS) ...
Scientists at the University College London (UCL) have developed a novel therapy that helps treat patients with T cell acute ...
Scientists at NYU Langone Health, its Perlmutter Cancer Center, and collaborators report that an activity pattern in certain genes responsible for building spleen tyrosine kinases can predict which ...