An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...
An Illinois family pushed for both boys to receive the potentially life changing medical treatment after one was approved and ...
The UAE has become the second country worldwide to approve Itvisma, a groundbreaking gene therapy for spinal muscular atrophy ...
There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College ...
X-linked retinoschisis gene replacement therapy, aiming to improve retinal architecture and visual function in young male ...
The treatment uses a modified, harmless virus to deliver healthy genes to a patient’s cells to treat genetic diseases. Read ...
There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...
Kids like David with SMA Type 1 typically don’t survive past the age of two. He may be the first to have gene therapy as ...
A small group of volunteers will receive multiple injections of the experimental treatments next month, says Unlimited Bio.
The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...
In the big picture, matched sibling donor transplants remain the standard of care, Boelens said. But gene therapy is ...
The first infant to undergo gene-editing therapy has accomplished another first — his first steps. KJ Muldoon is walking and ...